# Broadening applications for intrathecal gene therapy: a case for lysosomal storage diseases

**Authors:** eBioMedicine

PMC · DOI: 10.1016/j.ebiom.2026.106129 · 2026-01-14

## Full-text entities

- **Diseases:** lysosomal storage diseases (MESH:D016464)

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Source: https://tomesphere.com/paper/PMC12902244