# Targeting rare splicing defects: Antisense oligonucleotides offer a therapeutic strategy in FRDA

**Authors:** Laurie M.C. Kerkhof, Ronald A.M. Buijsen

PMC · DOI: 10.1016/j.omtn.2025.102723 · Molecular Therapy. Nucleic Acids · 2025-10-13

## Full-text entities

- **Diseases:** FRDA (MESH:D005621)

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Source: https://tomesphere.com/paper/PMC12550291