# In vivo adeno-associated virus-mediated LDLR/PCSK9 intervention for familial hypercholesterolemia

**Authors:** Zeyu Han, Cheng Tan, Jianzhong Ai, Ye Zhu

PMC · DOI: 10.1016/j.gendis.2025.101632 · Genes & Diseases · 2025-04-10

## Full-text entities

- **Genes:** PCSK9 (proprotein convertase subtilisin/kexin type 9) [NCBI Gene 255738] {aka FH3, FHCL3, HCHOLA3, LDLCQ1, NARC-1, NARC1}, LDLR (low density lipoprotein receptor) [NCBI Gene 3949] {aka LDLCQ2}
- **Diseases:** familial hypercholesterolemia (MESH:D006938)
- **Species:** Adeno-associated virus (species) [taxon 272636]

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## References

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Source: https://tomesphere.com/paper/PMC12281168